Posts about hemophilia


Gene Therapy by L.E. Carmichael - Front Cover

Introduction to Gene Therapy: It Sounds Simple, But It’s Sure Not Easy

Muscular dystrophy, hemophilia, Leber congenital amaurosis (LCA), cancer... they all have one thing in common. They are genetic diseases, ultimately caused by missing or malfunctioning genes in the patient's DNA. Until recently, we could treat the symptoms of many ... Read More