Today, we're talking about the second major challenge with gene therapy - getting replacement DNA into EVERY affected cell in a patient's body - and why that problem leads to the central ethical debate in this field. Read More
Gene therapy involves repairing or replacing a faulty gene that has led to disease. In order to do that, one major hurdle must be overcome: getting new DNA into the patient's cells. Cells, however, are designed to keep things ... Read More
Muscular dystrophy, hemophilia, Leber congenital amaurosis (LCA), cancer... they all have one thing in common. They are genetic diseases, ultimately caused by missing or malfunctioning genes in the patient's DNA. Until recently, we could treat the symptoms of many ... Read More