Posts about National Organization for Rare Disorders


Gene Therapy by L.E. Carmichael - Front Cover

Gene Therapy Research Gets Stamp of Approval

In it’s simplest form, gene therapy involves replacing disease-causing variants of genes with healthy ones, in order to¬†reduce or eliminate the symptoms of the condition. “Simple” in this context is extremely deceptive, however, as the process is¬†extremely complex and ... Read More